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e-book: Sapropterin dihydrochloride for the management of phenylketonuria: a guide for patients

e-book: Sapropterin dihydrochloride for the management of phenylketonuria: a guide for patients
  • Endocrinology and metabolism
  • Phenylketonuria (PKU)

Resource type

Slide kit

Tags

sapropterin

Usage

Practical

Authors:

Margreet van Rijn
Karen Anjema
Esther van Dam
Foekje de Boer
Francjan van Spronsen


Introducing sapropterin into the management of someone’s PKU is a somewhat complex and sometimes challenging process, where working closely with their healthcare team is essential to ensure the best possible outcome for the person with PKU and their families or carers. This guide provides important information for people starting treatment with sapropterin, including how it works, how to know whether an individual responds to sapropterin, how treatment with sapropterin is started and how it is main- tained over the long term. We hope that you find this guide informative and interesting and a useful resource.

Terms of use

This is a copyrighted resource for the sole purpose of education. Resource may be used for classroom training only and must remain as is, including the branding and EXCEMED logo. It is backed by a publishing license, signed by the author.